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SMA: With pharmacotherapy, we restore patients to their potential

MedExpress Team

Published June 13, 2023 08:00

SMA: With pharmacotherapy, we restore patients to their potential - Header image
- Very many adults with SMA are active in the workforce and living full lives despite their disabilities. Regaining previously lost functionality realistically translates into their everyday life, e.g., they turn part-time jobs into full-time jobs, continue their education or pursue their hobbies," Prof. Anna Kostera-Pruszczyk, head of the Department of Neurology at UCK WUM, said in an interview with Medexpress.

For more than four years, Polish patients with SMA have benefited from treatment with nusinersen. How does the therapeutic program monitoring system evaluate the efficacy, safety and effects of this therapy?

Treatment with nusinersen was introduced in Poland under reimbursement in 2019. We are currently treating 820 patients, with a full cross-section of ages and varying degrees of symptom severity at the time of therapy initiation. Through the SMPT system, we continuously track the functional status of our patients on relevant scales. The results are unequivocally positive. Perhaps even above the expectations of those who wondere...

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